Sepiapterin (Sephience™) for Hyperphenylalaninemia (HPA) in Patients 1 Month and Older with Sepiapterin-Responsive Phenylketonuria (PKU)

Welcome to BC PharmaCare's public survey of drugs being reviewed for coverage. This survey is for sepiapterin (Sephience) for the treatment of hyperphenylalaninemia (HPA) in adult and pediatric patients 1 month of age and older with sepiapterin-responsive phenylketonuria (PKU). Sepiapterin is indicated in conjunction with a phenylalanine (Phe)-restricted diet.

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